AGE-RELATED MACULAR DEGENERATION TREATMENT |
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| 申请号 | US15964584 | 申请日 | 2018-04-27 | 公开(公告)号 | US20180320180A1 | 公开(公告)日 | 2018-11-08 |
| 申请人 | BENITEC BIOPHARMA LIMITED; | 发明人 | David SUHY; Tin MAO; Shih-Chu KAO; | ||||
| 摘要 | This invention is directed to an RNA interference (RNAi) agent and the use of that RNAi agent to treat Age-related Macular Degeneration, as well as pharmaceutical compositions containing the RNAi agents of the invention. The RNAi agent is a DNA-directed RNA interference (ddRNAi) agent (being an RNA molecule), together with an expression cassette or construct to express that agent in a cell (including in vivo), for inhibiting, preventing or reducing expression of an AMD associated gene. Preferably that AMD associated gene is one that is associated with wet AMD. | ||||||
| 权利要求 | |||||||
| 说明书全文 | |||||||
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